41 Best Gene Therapy Doctors near Assi, Varanasi

Gene therapy is a research-based therapy in which genes can be modified to prevent and treat genetic diseases. Genetic material is introduced into human cells for the compensation of abnormal genes. In future, this technique may replace drugs or surgery.

Cancer, heart diseases, diabetes, cystic fibrosis, AIDS, haemophilia, etc. are some of the diseases that can be treated with gene therapy in future. The therapy is still in the research stage in the United States.

Germline therapy and somatic gene therapy are two general types of gene therapy. Germline therapy involves modifying genes inside the germ cells (ova or sperm). In somatic gene therapy, therapeutic DNA is inserted into body cells (not the germ cells).

There are different approaches related to gene therapy treatment. These are inactivating a mutated gene that functions improperly, inserting a healthy copy of a mutated gene or introducing a new gene into the target tissue in the body.

Gene therapy is presently available in a research setting. The U.S. Food and Drug Administration (FDA) has approved only a restricted number of gene therapy products. Several clinical trials are underway for testing this therapy as a treatment mode for diseases.